Home

News

Here you'll find all the latest information on Rett Syndrome research, Reverse Rett and other news that impacts our community.

UK Clinical Trial update

 

March 2018

There had never been a clinical trial of a potential treatment for Rett Syndrome in the UK until the Sarizotan trial started at the Clinical Research Facility, King’s College Hospital in London last year.

The drug is being trialled...

Cognitive Function in Rett Syndrome: Where are we at?

By Dr. J Singh, MSc, PhD

How do we measure cognition? Typically, standardized tests which require verbal responses can be used. As a young child I had first-hand experience of these tests. My communication was severely limited and so I was exposed...

AveXis Reports on Rett Gene Therapy Program

In June of 2017 AveXis announced that based on encouraging data generated by RSRT’s Gene Therapy Consortium it would advance the lead MECP2 gene therapy candidate toward clinical trials.

On 28th February 2018 the company provided an update on its...

Rare Disease Day: Only you

By Rachael Stevenson

It’s International Rare Disease Day today and the theme this year is research. Research is important to anyone affected by a rare disease and anyone affected knows why. Only research will ultimately bring about treatments and...

Page 1 of 32 pages