research happenings

Update on Cannabinoids from Dr Ram Kumar

Dr Ram Kumar at a recent meeting of the Rett Disorders Working Group

Following the heart-breaking case of Billy Caldwell, there has been widespread media coverage of cannabinoid medicines and their potential to treat epilepsy.

None of this was...

Cannabis based treatments: what’s happening now?

There have been a number of stories in the news recently about children whose families have been using cannabis-based treatments for epilepsy.

‘Cannabis-based treatments’ can mean a lot of different things.

As most people know, cannabis itself, is...

Meet a leading Rett researcher



Ralph Hector is a geneticist who is working hard in search of our cure. Andy recently caught up with Ralph to find out what he has been working on and to show you the impact your support is making. 


Andy: Ralph thanks for making time to...

UK Clinical Trial update


March 2018

There had never been a clinical trial of a potential treatment for Rett Syndrome in the UK until the Sarizotan trial started at the Clinical Research Facility, King’s College Hospital in London last year.

The drug is being trialled...

AveXis Reports on Rett Gene Therapy Program

In June of 2017 AveXis announced that based on encouraging data generated by RSRT’s Gene Therapy Consortium it would advance the lead MECP2 gene therapy candidate toward clinical trials.

On 28th February 2018 the company provided an update on its...

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