research happenings

AveXis Reports on Rett Gene Therapy Program

In June of 2017 AveXis announced that based on encouraging data generated by RSRT’s Gene Therapy Consortium it would advance the lead MECP2 gene therapy candidate toward clinical trials.

On 28th February 2018 the company provided an update on its...

UK Rett Disorders Working Group update

By Rachael Stevenson

The UK Rett Disorders Working Group met on the 6th of December 2017 in Covent Garden, London. The group comprised of the following individuals:

Hilary Truss, Rachael Stevenson, Judith Sheppard, John Sharpe,  Becky Jenner (Rett...



Guest blog post by Gael Gordon PhD.

This week for the first time, I appeared in the Sun.  I would like to make it clear that this was never on my bucket-list but getting the news about Rett Syndrome sometimes means doing stuff like this.  The...

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